Publications

Overview of AL Amyloidosis

The Amyloidosis Forum: a public private partnership to advance drug development in AL amyloidosis

Lousada and The Inaugural Amyloidosis Forum Panelists, Orphanet Journal of Rare Diseases (2020) 15:268

The Amyloidosis Forum: A Public-Private Partnership to Advance Drug Development in AL Amyloidosis

Isabelle Lousada, Vaishali  Sanchorawala, Angela Dispenzieri, Kristen Hsu, Robyn Himick, Preston Dunnmon, Mathew Maurer. International Society of Amyloidosis, Annual Meeting 2020

 

Novel Endpoints and Analyses

Proposed Cardiac End Points for Clinical Trials in Immunoglobulin Light Chain Amyloidosis: Report From the Amyloidosis Forum Cardiac Working Group

Mathew S Maurer, Preston Dunnmon, Mariana Fontana, Christina Candida Quarta, Krishna Prasad, Ronald M. Witteles, Claudio Rapezzi, James Signorovitch, Isabelle Lousada, Giampaolo Merlini, Circulation: Heart Failure, 121.009038, March 2022

Evaluation of NT-proBNPas surrogate endpoint in AL amyloidosis: development of a platform for federated, multi-institution meta-analysis of randomized trials

Angela Dispenzieri, James Signorovtich, Mathew S. Maurer, Xianghua Huang, Vaishali Sanchorawala, Preston Dunnmon, Catherine Klersy, Giulia Gambini, David Brown, Yolanda Barbachano, Rosalyn Adigun, Kristen Hsu, Isabelle Lousada, Liang Xiu, Douglas V. Faller, Richard Labotka, Giampaolo Merlini, Giovanni Palladini. XVIII Meeting of the International Society of Amyloidosis, 2022

Health-Related Quality of Life Instruments for Clinical Trials in AL Amyloidosis: Report from the Amyloidosis Forum HRQOL Working Group

Rizio AA, White MK, D’Souza A, Hsu K, Schmitt P, Quock TP, Signorovitch J, Lousada I, Sanchorawala V. Health-Related Quality of Life Instruments for Clinical Trials in AL Amyloidosis: Report from the Amyloidosis Forum HRQOL Working Group. Patient Relat Outcome Meas. 2023 May 18;14:153-169. doi: 10.2147/PROM.S399658. PMID: 37229285; PMCID: PMC10202704.

Peripheral Nervous, Hepatic, and Gastrointestinal Endpoints for AL Amyloidosis Clinical Trials: Report from the Amyloidosis Forum Multi-organ System Working Group

Mauermann ML, Clarke JO, Litchy WJ, Obici L, Lousada I, Gertz MA; Amyloidosis Forum Working Group Participants. Peripheral Nervous, Hepatic, and Gastrointestinal Endpoints for AL Amyloidosis Clinical Trials: Report from the Amyloidosis Forum Multi-organ System Working Group. Adv Ther. 2023 Nov;40(11):4695-4710. doi: 10.1007/s12325-023-02637-4. Epub 2023 Sep 2. PMID: 37658177; PMCID: PMC10567953.