Agenda

Agenda

8:00 am Registration Opens

9:00 am Welcome 
Isabelle Lousada, CEO & President, Amyloidosis Research Consortium

9:05 am Opening Remarks 
Preston Dunnmon, MD, Cardiologist DCRP

Session 1: Overview of AL Amyloidosis

Moderator: Mat Maurer, MD PhD, Arnold and Arlene Goldstein Professor of Cardiology; Professor of Medicine, Columbia University Medical Center

9:15 am Pathobiology and Clinical Features 
Raymond Comenzo, MD, Director, Transfusion Services; Director, John C. Davis Myeloma and Amyloid Program; Professor, Tufts University School of Medicine

9:35 am Epidemiology
Angela Dispenzieri, MD, Consultant; Division of Hematology; Serene M. and Frances C. Durling Professor of Medicine and of Laboratory Medicine and Pathology; Hematology Research Chair – Mayo Clinic College of Medicine. President of the International Society of Amyloidosis

9:45 am Study Populations and Staging Systems 
Angela Dispenzieri, MD, Consultant; Division of Hematology; Serene M. and Frances C. Durling Professor of Medicine and of Laboratory Medicine and Pathology; Hematology Research Chair – Mayo Clinic College of Medicine. President of the International Society of Amyloidosis

10:15 am Panel Discussion 

11:00 am Break

11:20 am Quality of Life 
Vaishali Sanchorawala, MD, Director, Amyloidosis Center – Boston University School of Medicine and Boston Medical Center

11:30 am Panel Discussion 

11:40 am FDA Approach to Multisystemic Diseases
Preston Dunnmon, MD, Cardiologist, Division of Cardiovascular and Renal Products (DCRP) Melanie Blank, MD, Nephrologist, Rare Diseases Program OND IO Michelle Campbell, PhD, Senior Clinical Analyst, Division of Neurology Products (DNP) Nicole Gormley, MD, Multiple Myeloma Clinical Team Leader Jessica Lee, MD, Associate Director, Division of Gastroenterology and Inborn Errors Products (DGIEP) Kimberly Smith, MD, Nephrology, Division of Cardiovascular and Renal Products (DCRP)
12:10 pm Q+A 
12:40 pm Lunch 

Session 2: Challenges in Clinical Trial Design

Moderator: Vaishali Sanchorawala, MD, Director, Amyloidosis Center – Boston University School of Medicine and Boston

1:20 pm Patient Perspectives 
Isabelle Lousada and 2 patients

1:40 pm Challenges Designing Trials with Newly Diagnosed Patients 
Ashutosh Wechalekar, MBBS, MD, FRCP, FRCPath, DM, Professor of Medicine and Haematology, Hon. Consultant, National Amyloidosis Centre, University College London (Royal Free Campus); Dept of Haematology, Royal Free Hospital; Dept of Haematology, University College Hospital, London

1:55 pm Challenges Designing Trials with Relapsed/Refractory Patients 
Heather Landau, MD, Hematologist/Oncologist, Memorial Sloan KetteringCancer Center

2:10 pm Panel Discussion 
3:10 pm Roadmap for Future Discussions 
Preston Dunnmon

3:40 pm Closing Remarks 
Isabelle Lousada and Preston Dunnmon

3:50 pm Adjourn